May 21, 2017
Project Alive: Documentary Series and Social Media Challenges Seek to Raise MPS Awareness
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September 3, 2016
ArmaGen Presents Data from First Cohort of Phase 1/2a of AGT-182 for Treatment of Hunter Syndrome
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March 17, 2016
Abeona Therapeutics Announces FDA Allowance of Investigational New Drug for Patients With Sanfilippo Syndrome Type A (MPS IIIA)
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June 11, 2015
The Times of India (Bangalore): Court Orders “Treat Rare Disease Patients for Free”
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September 30, 2013
UAB Researcher Answered Questions for Families of Children with Rare Diseases
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May 17, 2013
Orphans No More: Renaissance in New Drugs for Rare Diseases
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January 10, 2012
Charity Tuesday: Courage to Make a Difference
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September 13, 2011
A RARE DISEASE PATIENT PERSPECTIVE – Roy Zeighami
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August 18, 2011
Genzyme Announces Winners of Patient Advocacy Leadership Award Grants
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April 20, 2011
San Francisco Giants to host Rare Disease Fundraiser for MPS IV – with YouTube sensation Keenan Cahill!
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October 27, 2010
Former BioMarin exec targets orphan drugs
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