Tag: Neimann Pick

A total of 6 posts are filed under Neimann Pick
Vtesse Granted Breakthrough Therapy Designation for Neimann-Pick
Vtesse, Inc., which launched in January 2015, is the first spin-off company for orphan drug accelerator, Cydan Development, Inc who today… Continue Reading
Blog Hop for Rare Disease Day – Please Read, Share and Raise Awareness!
There are less than 30 days to World Rare Disease Day on February 29. We kick off our campaign this year as host of a Rare Disease Blog Hop.… Continue Reading
Washington Post Supplement sheds light and insights into the world of rare disease
Many Advocates, Industry, Parents, Advocacy Organizations have participated in the first in a series of Rare Disease reports being produced… Continue Reading
PARENT DRIVEN RESEARCH – Innovations from the trenches!
A Push to spur more drugs for deadly rare diseases LAURAN NEERGAARD, AP Medical Writer Cassidy Hempel, 6, waves at hospital staff with the… Continue Reading
Kids Helping Kids – Denim Ribbon’s being made to support World Rare Disease Day!
Over 50 kids and their families descended upon the RARE Offices to help make denim ribbons in preparation for World Rare Disease Day taking… Continue Reading
Children’s Hospital Oakland Receives FDA Clearance to Begin World’s First Cyclodextrin Administration Into the Brains of Twins with Rare and Deadly Cholesterol Disease
Sugar Molecule Used in Common Food and Household Products Like Febreze® Fabric Refresher Called Hydroxypropyl Beta Cyclodextrin (HPßCD)… Continue Reading