December 2, 2020
Fenrici Backpacks: Lessons in Resilience
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October 5, 2020
It’s Never Too Late to Find your Community
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June 17, 2020
Highlights from 2020 RARE Drug Development Symposium
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March 30, 2020
We’re All In This Together
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March 23, 2018
A Task for Tyler- Finding Treatments for SSADH and Hypotonia
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March 19, 2018
2q23.1 Diagnosis Leads Mom to Start Online Boutique for Daughter’s Future
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March 15, 2018
Ionis and Akcea Form hATTR Partnership Worth up to $1.7 Billion
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March 15, 2018
Flagship Pioneering Backs Foghorn Therapeutics with $50 Million to Develop New Class of Drugs to Regulate Genes
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March 12, 2018
Sanofi Passes on Alnylam Primary Hyperoxaluria Type 1 Candidate
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March 12, 2018
Sarepta Therapeutics Plans to Submit DMD Drug Golodirsen for FDA Approval by Year End
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