Tag: Sanfilippo Syndrome Type A

A total of 3 posts are filed under Sanfilippo Syndrome Type A
453 Days and Counting For Family in Quarantine
On Tuesday, Glenn O’Neill crossed off the number 453 from a large white sheet of paper hanging in the kitchen of his Columbus, South… Continue Reading
Lysogene Recieves US Orphan Designation for its Lead Intracerebral Gene Therapy Product SAF-301
LYSOGENE announced today that the U.S. Food and Drug Administration (FDA) has granted orphan drug designation to its lead gene therapy… Continue Reading
Battling Sanfilippo Syndrome Type A – Reed’s Story
In January of 2011, we learned that our then three and a half year old son Reed has Sanfilippo Syndrome Type A, a rare and fatal… Continue Reading
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