May 24, 2019
FDA Approves Gene Therapy Zolgensma for SMA; Novartis Sets Price at $2.1 Million
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May 10, 2017
Hope For 16-Year-Old California Boy Fighting Rare Genetic Disease
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February 17, 2017
RARECast: Moving Rare Disease Therapies from Hope to Reality
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January 25, 2017
Four-Year-Old with Amyotrophic Lateral Sclerosis Finds Hope With New Drug
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January 5, 2017
SPINRAZA™ (nusinersen) Approved in U.S. to Treat Broad Range of Patients with Spinal Muscular Atrophy
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January 3, 2017
Boy Battling Spinal Muscular Atrophy Takes First Steps
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November 28, 2016
A Family Secret: The Disease Our Doctors Have Yet to Understand
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April 15, 2016
RARECast: New Means of Regulating Genes May Hold Promise for Rare Disease Patients
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December 16, 2015
Taylor Stein’s New Documentary Reveals Son with Spinal Muscular Atrophy
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November 7, 2015
Santa Barbara Marathon to be Run in Honor of Gwendolyn Strong
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September 10, 2015
Annual Sacramento Walk & Roll for Spinal Muscular Atrophy, Oct 17th
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August 24, 2015
The Legacy of Gwendolyn Strong: Championing the SMA Community For All Patients
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