Tag: Synageva

A total of 4 posts are filed under Synageva
Rare Disease Report: FDA Approves Alexion’s Kanuma for LAL Deficiency
The FDA approved Alexion’s Kanuma (sebelipase alfa) to treat patients with lysosomal acid lipase (LAL) deficiency. Kanuma is an enzyme… Continue Reading
Synageva BioPharma Joins NORD, Eurordis and Global Genes Project in Support of Rare Disease Day 2013
Synageva BioPharma Corp. (Synageva), a clinical stage biopharmaceutical company developing therapeutic products for rare diseases, joins the… Continue Reading
Faircraft Records/Universal Republic Recording artist Chris Mann and Singer/Songwriter Katrina Parker to Perform at Global Genes | R.A.R.E Project’s Tribute to Champions of Hope™ Benefit
FOR IMMEDIATE RELEASE Actors Jason George, Nestor Serrano and Meagan Tandy will Serve as Celebrity Award Presenters; Henri Termeer, Former… Continue Reading
Clinical Development Program in LAL Deficiency By Synageva
LAL Deficiency, a lysosomal storage disorder, has early and late onset phenotypes, also referred to as Wolman Disease or Cholesteryl Ester… Continue Reading