Tag: treatments

A total of 5 posts are filed under treatments
Therapy May Curb Kidney Deterioration in Patients With Rare Disorder, Methylmalonic Acidemia
July 29, 2013 — A team led by researchers at the National Institutes of Health has overcome a major biological hurdle in an effort to… Continue Reading
Forbes: The Lifesaving Promise of the Pharmaceutical Drug Pipeline
There was a time not long ago when patients suffering from rare diseases had little hope of finding a medicine that could cure their ills.… Continue Reading
The Myelin Repair Foundation Aims to Eliminate The Valley of Death
What a great video. Watch to learn why $139 billion dollars invested into medical research only leads to 21 FDA approved drugs. The Myelin… Continue Reading
AKU Society joins forces with Partnership for Cures to find AKU treatments
The AKU Society has joined forces with US charity Partnership for Cures in order to develop and fund clinical trials into treatments for… Continue Reading
Tailoring Treatments for Kids; Perspectives Podcast Series a discussion with Don Lombardi
In treating pediatric patients, doctors and hospitals are often limited by available devices or drugs that have not been optimized for the… Continue Reading

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