RARE Toolkits

Below is a list of all of our current RARE Toolkits.



T8 10

This Global Genes™ Toolkit will provide you with an overview of how new drugs are developed and approved in the U.S. and describe the differences when developing new drugs for rare diseases.

This Toolkit is one in a Global Genes series on drug development, From Molecules to Medicine, with others in the series providing more detail on each step of the process. In this Toolkit, we will take a look at each of the steps in the drug development process, outline differences in drug development for rare diseases, and discuss why now, more than ever before, the rare disease community can be optimistic about the development of new treatments. Our goal is to provide you with the information you need to better understand and participate more effectively in the development of treatments for rare diseases.