RARE Drug Development Symposium: Government Funding Resources Workshop

December 15, 2020

Dr. P.J. Brooks, Dr. Sean Ekins, and Dr. David Wright discuss how patient groups are able to optimize government funding for rare disease research.

Lisa Kadyk & Aditi Desai from CIRM talk about being at Week in RARE

Lisa Kadyk, PhD, Associate Director of Therapeutics, and Aditi Desai, MPH, CPH, Community Outreach Manager, at CIRM, […]

Learn what newborn screenings are, why they are important, how regulations vary by states across the U.S., […]

Updated to include an article about Beyoncé stepping up to get a fan in a wheelchair to […]

During this webinar presented with IN-PART, Karmen Trzupek, Senior Director of Scientific Programs at Global Genes, shared […]

Rare drug development cannot move forward, or move forward quickly without collaboration. The ecosystem works best when […]

Panelists from the 2023 RARE Drug Development Symposium discuss how patient advocacy organizations can be research ready, […]

To answer the question of HOW patient advocates can be involved in rare drug development, we must […]

Today’s rare disease advocates are on the forefront of drug development – whether in fundraising, raising awareness, […]

Charlene Son Rigby, CEO of Global Genes, talks about rare drug development, how patient advocates can contribute […]