RARE Drug Development Symposium: Translational Steps Academia to Industry

December 15, 2020

Hear Dr. Ethan Perstein and Dr. Tamar Grossman discuss how patient-led activities and rare disease research in academia are able to be effectively translated to industry-level drug development efforts.

Deals

Lisa Kadyk & Aditi Desai from CIRM talk about being at Week in RARE

Lisa Kadyk, PhD, Associate Director of Therapeutics, and Aditi Desai, MPH, CPH, Community Outreach Manager, at CIRM, […]

Diagnosis

September is Newborn Screening Awareness Month

Learn what newborn screenings are, why they are important, how regulations vary by states across the U.S., […]

Diagnosis

The Not-So-Friendly Skies: Flying When You Have a Rare Disease

Updated to include an article about Beyoncé stepping up to get a fan in a wheelchair to […]

Drug Development

Virtual Partnering Event: IN-PART & Global Genes/RARE-X

During this webinar presented with IN-PART, Karmen Trzupek, Senior Director of Scientific Programs at Global Genes, shared […]

Diagnosis

Why Is Collaboration Important in Rare Therapy Development and Research?

Rare drug development cannot move forward, or move forward quickly without collaboration. The ecosystem works best when […]

Diagnosis

How Can Patient Organizations Be Research Ready?

Panelists from the 2023 RARE Drug Development Symposium discuss how patient advocacy organizations can be research ready, […]

Diagnosis

How Can Patient Advocates Be Involved in Rare Therapy Development?

To answer the question of HOW patient advocates can be involved in rare drug development, we must […]

Diagnosis

How Does Global Genes Support Advocates Looking to Expand Research Programs?

Today’s rare disease advocates are on the forefront of drug development – whether in fundraising, raising awareness, […]

Diagnosis

CEO Charlene Son Rigby Talks Drug Development and the Rare Research Roadmap

Charlene Son Rigby, CEO of Global Genes, talks about rare drug development, how patient advocates can contribute […]

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RARE Drug Development Symposium: Translational Steps Academia to Industry

Related

Lisa Kadyk & Aditi Desai from CIRM talk about being at Week in RARE

September is Newborn Screening Awareness Month

The Not-So-Friendly Skies: Flying When You Have a Rare Disease

Virtual Partnering Event: IN-PART & Global Genes/RARE-X

Why Is Collaboration Important in Rare Therapy Development and Research?

How Can Patient Organizations Be Research Ready?

How Can Patient Advocates Be Involved in Rare Therapy Development?

How Does Global Genes Support Advocates Looking to Expand Research Programs?

CEO Charlene Son Rigby Talks Drug Development and the Rare Research Roadmap

Stay Connected