Welcome, Opening Remarks and Keynote Presentation – Collaborations, Community and Citizen Science

Keynote Speaker: David Fajgenbaum, MD, MBA, MSc, Co-Founder & President, Castleman Disease Collaborative Network

Explore the evolution of patient-driven progress in research and the critical ways in which patients, advocates, and caregivers are changing the drug development paradigm. From patient engagement in endpoint design to adaptive clinical trial designs, hear insights on the changing landscape, what’s now, and what’s next in rare disease research.