Connexion Healthcare Celebrates WRDD with Local Fundraiser, Wear That You Care

PicMonkey Collage

Rare Disease Day is an international event held on the last day of February each year. The goals are to raise awareness about rare diseases and improve access to treatments and medical representation for individuals with rare and genetic diseases. In the United States, more than […]

The Most Important New Drug of 2012

Cystic Fibrosis Foundation

The Food and Drug Administration looks set for a great 2012.  With a few days left to go, it has approved 40 new drugs and vaccines, one of the most impressive totals ever, according to data from Pharmaceutical Approvals Monthly and FDA press releases. In […]

FDA User Fee Bill Is Landmark Legislation – Major Wins for the Rare Disease Patient Community Led by RDLA

RDLA is hosting an Advocates Luncheon & Conference Call on September 12, 2012.  RSVP is required for attendance.

Wednesday, June 27, 2012, Washington, DC — Rare Disease Legislative Advocates (RDLA) hails House and Senate passage of The Food and Drug Administration Safety and Innovation Act (FDASIA), S. 3187, landmark legislation that will encourage the development of new treatments for the 30 million Americans […]

Rare Disease Drugs: A $1 Trillion Market?

Matthew Herper The Medicine Show; FORBES November 2010 Right now drugs for rare disorders are the sweet spot of the biotechnology industry. Treatments for illnesses that affect only hundreds of patients can cost $200,000 or more and have built Genzyme into one of biotech’s biggest […]