Articles

Finance
January 25, 2022
Metagenomi Raises $175 Million to Advance Therapeutic Pipeline and Expand Gene Editing Platform
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Drug Development
January 25, 2022
FDA Grants Evrysdi Priority Review Based on Results from Treating Pre-Symptomatic Infants with SMA
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Drug Development
January 25, 2022
FDA Grants Rare Pediatric Disease Designation for Catalyst’s CB 4332 for Treatment of CFI Deficiency
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Drug Development
January 25, 2022
Sierra Oncology Reports Positive Results in Pivotal Trial of Momelotinib for Myelofibrosis
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Deals
January 25, 2022
Capricor and Nippon Shinyaku Partner to Commercialize and Distribute CAP-1002 to Treat DMD in U.S.
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Drug Development
January 24, 2022
FDA Tells Pfizer and OPKO It Won’t Approve Growth Hormone Therapy
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Drug Development
January 24, 2022
Ipsen Wins Approval for FOP Drug in Canada
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Drug Development
January 24, 2022
FDA Separately Grants Lantern Pharma and Codexis Rare Pediatric Disease Designations
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Drug Development
January 24, 2022
FDA Places Hold on Viking’s Phase 1b Trial of VK0214 in Patients with X-ALD
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RARECast Podcasts
January 21, 2022
Expanding the CRISPR Toolkit
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News

January 25, 2022
Finding Answers Through Genetic Testing – A ...
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January 11, 2022
Hearing Hoofbeats – Cox Scholarship winner, ...
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January 11, 2022
Going the Extra Mile – Cox Scholarship winne...
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January 11, 2022
Through the Eyes of a Patient – Cox Scholars...
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December 20, 2021
2021 Platforms of Hope – Realizing the Potential...
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August 12, 2021
Global Genes Grant Awardee Achieves Goal of Design...
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