Articles
BrainStorm Cell Will Submit BLA to FDA after New Analysis of Trial Results
Read More
Resilience Collaborates with Mayo to Manufacture and Deliver Biotherapeutics for Rare and Complex Conditions
Read More
Transforming the Treatment of Neuromuscular Diseases with Next-Gen Oligonucleotides
Read More
Novartis Reports Two Patient Deaths After Treatment with Zolgensma Gene Therapy
Read More
Raising Capital Remained Tough for Rare Disease Therapeutics Drug Developers in July
Read More
Disc Medicine Enters Reverse Merges with Gemini Therapeutics for Public Listing
Read More
ProQR Winds Down Clinical Trials to Focus Exclusively on Axiomer RNA-editing Technology
Read More
News
Social
RT @CFUCDF: Help us reach our goal🦓❤️@HorizonNews @ultragenyx @GlobalGenes @EveryLifeOrg @remember_girls @VitafloUSA @nord @Tr…
RT @GlobalGenes: “The organization is driven by the frustration that a lot of rare disease families...
RT @GlobalGenes: Podcaster, author and an inspiration to many. Hear how @KyleABryant’s cross-country bike ride changed...
