Articles
Krystal Biotech Raises $200 Million in Public Offering to Advance Redosable Gene Therapies
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AviadoBio Raises $80 million to Advance Neurodegenerative Gene Therapy Platform
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Astellas and Dyno Partner to Develop Next-Generation AAV Gene Therapy Vectors for Skeletal and Cardiac Muscle
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Tune Therapeutics Launches with Epigenomic Control Platform to Master Gene Networks
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GBT Grants $400,000 to Help Expand Sickle Cell Real-World Data Gathering in United States
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Vertex Reports Positive Results from Phase 2 Study of VX-147 in APOL1-Mediated FSGS
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Neuvivo Launches to Develop and Market Effective and Safe Treatments for ALS
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FDA Issues Draft Guidance on Use of Registries to Support Regulatory Decision-Making
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