Articles

Finance
August 16, 2022
Fulcrum Raises $75 Million in Public Offering to Advance Rare Disease Pipeline
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Drug Development
August 16, 2022
BrainStorm Cell Will Submit BLA to FDA after New Analysis of Trial Results
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Deals
August 16, 2022
Resilience Collaborates with Mayo to Manufacture and Deliver Biotherapeutics for Rare and Complex Conditions
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RARECast Podcasts
August 12, 2022
Transforming the Treatment of Neuromuscular Diseases with Next-Gen Oligonucleotides
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Drug Development
August 12, 2022
Novartis Reports Two Patient Deaths After Treatment with Zolgensma Gene Therapy
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Finance
August 11, 2022
Raising Capital Remained Tough for Rare Disease Therapeutics Drug Developers in July
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Finance
August 11, 2022
Disc Medicine Enters Reverse Merges with Gemini Therapeutics for Public Listing
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Strategy
August 11, 2022
ProQR Winds Down Clinical Trials to Focus Exclusively on Axiomer RNA-editing Technology
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Pricing
August 10, 2022
Pfizer Introduces Warranty Program for Rare Disease Drug Panzyga
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Finance
August 10, 2022
Mirum Raises $80 Million in Public Offering of Common Stock
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News

July 27, 2022
RARE Global Advocacy Alliance Member Spotlight: Ai...
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July 15, 2022
A mama’s heart showing the world differences...
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July 14, 2022
Helping Hands for GAND Hosts 3rd Biennial Gatherin...
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