Articles

Deals
October 25, 2021
CANbridge and Stitchr Global Collaborate to Develop Gene Therapy for Dystrophinopathies
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RARECast Podcasts
October 22, 2021
A Find-and-Replace Approach to Fixing the Mutation Underlying Sickle Cell Disease
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Healthcare
October 22, 2021
Medical Cost for Rare Diseases on Par with Cancer, Heart Failure
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Strategy
October 22, 2021
Bluebird Withdraws Gene Therapies in Europe as it Winds Down Operations There
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Rare Advocate
October 21, 2021
Rare Leader: Erica Webster, Co-Founder and President, Hope for Hypothalamic Hamartomas
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Finance
October 21, 2021
Crinetics Raises $150 Million in Public Offering to Advance Rare Endocrine Disease Pipeline
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Finance
October 21, 2021
ReCode Raises $80 Million to Advance Pipeline of Rare Lung Diseases Therapies
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Finance
October 21, 2021
FDA Awards Castle Creek $1.8 Million Grant to Support Pivotal Study in RDEB
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Deals
October 21, 2021
Selecta and Genovis Enter License Agreement to Advance Next-Generation IgG Protease in Gene Therapy and Autoimmune...
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Research
October 21, 2021
Study Finds Potential to Repurpose Cancer Therapies to Treat Rare Diseases
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News

August 12, 2021
Global Genes Grant Awardee Achieves Goal of Design...
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August 3, 2021
RARE Foundation Alliance Member Spotlight: Jennife...
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July 9, 2021
RARE Foundation Alliance Member Spotlight: Ashley ...
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June 24, 2021
RARE Foundation Alliance Member Spotlight: Matt La...
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May 10, 2021
RARE Foundation Alliance Member Spotlight: Sharon ...
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April 5, 2021
RARE Foundation Alliance Member Spotlight: Allison...
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