Paroxysmal nocturnal hemoglobinuria
Synonyms: Marchiafava-Micheli disease | PNH
Paroxysmal nocturnal hemoglobinuria (PNH) is an acquired clonal hematopoietic stem cell disorder characterized by corpuscular hemolytic anemia bone marrow failure and frequent thrombotic events.
Data from Orphanet are used to provide information on a disease's name, synonym(s), and overview.
Reference: Access aggregated data from Orphanet at Orphadata.
Orphadata: Free access data from Orphanet. © INSERM 1999. Available on http: //www.orphadata.org. Data version June 2023.
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Paroxysmal nocturnal hemoglobinuria?
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