maltese_ rare
25,000 Maltese Citizens Suffer from a Rare Disease

(SOURCE) The Maltese government is promoting…

Parent’s Make Sure Child Experiences the World Before Krabbe Disease Takes Hold
By Amber McNamara and Tyson Williams Autumn Rose Williams was born August 3rd, 2016 with much anticipation. She was a perfect baby in… Continue Reading
Global Genes and EveryLife Foundation Announce First-Ever RARE on the Road – Rare Disease Leadership Tour
 Leading rare disease patient advocacy organizations Global Genes – Allies in Rare Disease and the EveryLife Foundation for Rare… Continue Reading
Eyes_Gene_Therapy
Allergan Signs Deal with Editas for Gene-Editing-Based Eye Treatments
Allergan plc said on Tuesday it would get exclusive access and the option to license up to five of Editas Medicine Inc’s experimental… Continue Reading
Napa In Newport
Napa In Newport Raises $1 Million To Help Find a Cure for Duchenne Muscular Dystrophy
More than 400 people gathered at the Ritz-Carlton on Saturday, March 4 to enjoy the nectar of top Napa Valley wineries and help find a cure… Continue Reading
Drunk without Drinking: Auto-Brewery Syndrome
by Dr. Barbara Cordell When my husband was 61 years old, he broke his foot, had to have surgery, and received antibiotics. Shortly… Continue Reading
Regenerative_Cell_Thera[y
InGeneron Completes Strategic Financing from Sanford Health to Advance Regenerative Cell Therapies
 InGeneron Inc., a regenerative medicine and cell therapy company, announces that Sanford Health, one of the largest integrated healthcare… Continue Reading
John_Walsh_Alpha_1
Honoring John W. Walsh’s Alpha-1 Legacy
John W. Walsh, whose vision of a research foundation and a patient services organization for people with Alpha–1 Antitrypsin Deficiency… Continue Reading