Related
Savara’s Early Access Program
Savara’s Early Access Program (EAP) for molgramostim inhalation solution (molgramostim) in Autoimmune Pulmonary Alveolar Proteinosis (Autoimmune […]
Read morePublication Announcement — RARE-X: Advancing Rare Disease Research Through Patient-Driven Data
Global Genes is excited to announce “RARE-X: A patient-driven approach for collecting symptom and patient-reported outcome data […]
Read moreAccelerating Rare Disease Research Through Collaboration: Global Genes and Notre Dame Launch the Research Acceleration Program
Global Genes and University of Notre Dame have partnered to launch the Research Acceleration Program, a collaborative […]
Read moreRARE Advocacy Exchange Session 8, Knowing Your Rare Rights
This session recording is from Oct. 16, 2025 Rare Advocacy Exchange Session 8: Knowing the Rights for […]
Read moreGlobal Genes Guide to Starting a Nonprofit Patient Advocacy Organization
This Global Genes Quick Guide is a resource for advocates focused on pressing topics causing challenges in […]
Read moreRARE Advocacy Exchange Session 7, Getting a Precise Genetic Diagnosis
This session recording is from Sept. 18, 2025 Rare Advocacy Exchange Session 7: Getting A Precise Diagnosis […]
Read moreRARE Advocacy Exchange Session 6 : Grieving a RARE Diagnosis
Rare disease grief differs from the grief we commonly associate with losing a loved one to death. […]
Read moreA Student’s Perspective: Lessons from the 2025 RARE Drug Development Symposium
During my first week as a Harvard College junior, I was delighted to be given the opportunity […]
Read moreGlobal Genes Guide to Genetic Diagnosis
This Global Genes Quick Guide is a resource for advocates focused on pressing topics causing challenges in […]
Read more
