Join us in person or online June 8-10 for the 2022 RARE Drug Development Symposium
in partnership with the Orphan Disease Center of the University of Pennsylvania.

The RARE Drug Development Symposium, in partnership with the 

Orphan Disease Center of the University of Pennsylvania, is designed to connect, educate, and inspire rare disease participants, whether they’re beginning or advanced. This program convenes key stakeholders across patient advocacy, research, and drug development to engage on emerging challenges, and new frameworks to advance rare disease research and therapeutic development. 

The 2022 Rare Drug Development Symposium will focus on “Disruptive Innovations in Rare Disease Research.” Registration will open Mar 7, 2022 with options for you to register to participate in person or virtually. Subscribe (scroll down to the yellow “Stay Connected” section!) to receive Global Genes communications, including an announcement when registration begins.

This year’s Symposium will include multiple tracks to help rare disease stakeholders grow in and gain a better understanding of the requirements of research in the rare disease space no matter their role – advocate, researcher, healthcare worker, investigator, industry, or patient/caregiver. Sessions will equip attendees to become confident and involved in rare disease research and understand the opportunities available for them in the space.

Foundational Workshops: Leading up to the June conference, Global Genes will host a series of virtual workshops to help attendees gain foundational knowledge on research and drug development topics. These sessions will allow attendees to come to the RARE Drug Development Symposium equipped to make the most of their time.. Check back later for a full list of workshop dates, or subscribe to receive Global Genes communications.

You can see highlights from the 2021 RARE Drug Development Symposium below, and click here for the RARE Drug Development Symposium 2021 Report.

2021 Rare Drug Development Symposium Highlights:

Download the 2021 Global Genes Drug Development Report

See highlights from the 2021 RARE Drug Development Symposium – Top Session Recommendations:

Welcome, Opening Remarks and Keynote Presentation – Collaborations, Community and Citizen Science

Welcome, Opening Remarks Day 2 and Seizing the Moment: Expanding Impact and Access in Translational Science

Equity & Ethics in Context – Raising the Bar for Access in Rare Disease

Pre Conference Workshop From Discovery to Approval – Understanding Pathways to Accelerate Therapeutics

Building a Research Strategy Roadmap for Your Organization

Deep Dive – Contextualizing Endpoints and Therapeutic Advances in Rare Disease

View the full list of 2021 Rare Drug Development Symposium recordings here.

From: 06/08/2022 - To: 06/10/2022

All day event

Virtual Event:

Bronze Sponsors

Industry-session Sponsor

General Sponsor