The RARE Research Roadmap – 2023 RARE Drug Development Symposium

In May 2023, Global Genes and the Orphan Disease Center of the University of Pennsylvania hosted the RARE Drug Development Symposium where Deborah Requesens, Director of the Orphan Disease Center, and Global Genes CEO Charlene Son Rigby explained the stops along the research roadmap. 

An overview of the end-to-end drug development process highlighting interconnection points where patient advocacy groups can contribute. This video helps you understand the flow of basic research, early-stage research, clinical trials, regulatory, commercialization, and post-market follow up.

Deborah Requesens, PhD
Director, JumpStart, Orphan Disease Center, University of Pennsylvania

Charlene Son Rigby
CEO, Global Genes

Wherever you are in your journey, whether newly diagnosed, managing your disease, involved in research, or participating in a clinical trial, Global Genes and the Orphan Disease Center can provide information to keep you on the right path.

RARE Disease Research Roadmap

Rare Research RoadMap