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If your rare disease is likely to have a clinical trial for a drug or treatment come […]
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Read moreGlobal Genes Statement on Current State of Affairs, Research Funding, and Federal Agency Impacts on Rare Disease
In times of change and uncertainty, it is especially important for individuals and families in the rare […]
Read moreWeek in Rare 2024 RARE Advocacy Summit sessions for Growing your Organization Research Readiness
The Global Genes Summit is known for bringing together those facing the challenges of rare disease life, […]
Read moreAmazon Web Services Commits $10 million to Pediatric Rare Disease Research & More — This Week in RARE Daily
This Week in RARE Daily is a feature from Global Genes where you can get a quick […]
Read moreThe need for regulators to exercise their flexibility to address ultra-rare therapies — 2024 NEXT Report
The path to rare disease drug development comes with built-in obstacles as it is, but when seeking […]
Read moreFDA Grants Sarepta Expanded Approval for DMD Gene Therapy & More — This Week in RARE Daily
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Read moreImproved Gene Editing System Makes Gene-Sized Edits & More — This Week in RARE Daily
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Read more2024 RARE Champions of Hope Nominees Announced
The RARE Champions of Hope Awards celebrate, honor and recognize those in the rare disease community who […]
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