How Can Patient Advocates Be Involved in Rare Therapy Development?

To answer the question of HOW patient advocates can be involved in rare drug development, we must first find out WHY they are involved. Is it to find a way to manage symptoms? Prolong life? What are some of the ways that advocates are becoming involved in rare drug development? How can they influence drug development?

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This video includes interviews that were filmed at the 2023 RARE Drug Development Symposium, May 1-3 in Philadelphia, Pennsylvania. For more information about this event, or to become involved in next year’s event, please visit https://globalgenes.org/event/rare-disease-drug-development/