Advances in Rare Immunological Diseases

September 11, 2020

Recent advances in rare immunological diseases have raised the exciting potential of cures for some disorders. Hear from experts about what advances in gene and cell therapies might mean for patients.

Speakers: Manish Butte, MD, PhD & Claudia Gonzaga-Jauregui

Deals

Lisa Kadyk & Aditi Desai from CIRM talk about being at Week in RARE

Lisa Kadyk, PhD, Associate Director of Therapeutics, and Aditi Desai, MPH, CPH, Community Outreach Manager, at CIRM, […]

Diagnosis

September is Newborn Screening Awareness Month

Learn what newborn screenings are, why they are important, how regulations vary by states across the U.S., […]

Diagnosis

The Not-So-Friendly Skies: Flying When You Have a Rare Disease

Updated to include an article from USA Today (September 18, 2023) Daniel DeFabio. Director of Community Engagement […]

Drug Development

Virtual Partnering Event: IN-PART & Global Genes/RARE-X

During this webinar presented with IN-PART, Karmen Trzupek, Senior Director of Scientific Programs at Global Genes, shared […]

Diagnosis

Why Is Collaboration Important in Rare Therapy Development and Research?

Rare drug development cannot move forward, or move forward quickly without collaboration. The ecosystem works best when […]

Diagnosis

How Can Patient Organizations Be Research Ready?

Panelists from the 2023 RARE Drug Development Symposium discuss how patient advocacy organizations can be research ready, […]

Diagnosis

How Can Patient Advocates Be Involved in Rare Therapy Development?

To answer the question of HOW patient advocates can be involved in rare drug development, we must […]

Diagnosis

How Does Global Genes Support Advocates Looking to Expand Research Programs?

Today’s rare disease advocates are on the forefront of drug development – whether in fundraising, raising awareness, […]

Diagnosis

CEO Charlene Son Rigby Talks Drug Development and the Rare Research Roadmap

Charlene Son Rigby, CEO of Global Genes, talks about rare drug development, how patient advocates can contribute […]

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Advances in Rare Immunological Diseases

Related

Lisa Kadyk & Aditi Desai from CIRM talk about being at Week in RARE

September is Newborn Screening Awareness Month

The Not-So-Friendly Skies: Flying When You Have a Rare Disease

Virtual Partnering Event: IN-PART & Global Genes/RARE-X

Why Is Collaboration Important in Rare Therapy Development and Research?

How Can Patient Organizations Be Research Ready?

How Can Patient Advocates Be Involved in Rare Therapy Development?

How Does Global Genes Support Advocates Looking to Expand Research Programs?

CEO Charlene Son Rigby Talks Drug Development and the Rare Research Roadmap

Stay Connected