Deals Profluent Releases AI-Created and Open-Source Gene Editor & More — This Week in RARE Daily This Week in RARE Daily is a feature from Global Genes where you can get a quick […] Read more
Deals Expanding Access to Genome Sequencing in Rural Populations & More — This Week in RARE Daily This Week in RARE Daily is a feature from Global Genes where you can get a quick […] Read more
Deals Financings of Public Rare Disease Drug Developers Soar & More — This Week in RARE Daily This Week in RARE Daily is a feature from Global Genes where you can get a quick […] Read more
Deals Promise and Challenges of Gene-Editing and Other Genomic Medicines — 2024 NEXT Report When scientists completed the Human Genome Project in 2003, it provided, among other things, a reference genome […] Read more
Deals NCATS Seeks Applicants for Rare Disease Clinical Research Funding & More — This Week in RARE Daily This Week in RARE Daily is a feature from Global Genes where you can get a quick […] Read more
Deals Celebrating the Most Expensive Drug for the Disease You Never Heard Of & More — This Week in RARE Daily This Week in RARE Daily is a feature from Global Genes where you can get a quick […] Read more
Deals FDA Approves First Gene Therapy for Children with MLD & More — This Week in RARE Daily This Week in RARE Daily is a feature from Global Genes where you can get a quick […] Read more
Deals Rare, Ultra-Rare & Hyper-Rare: A Search for Paths Forward — 2024 NEXT Report Over 40 years after the Orphan Drug Act of 1983, the definition of rare disease as it […] Read more
Living with a RARE Disease Recapping Global Genes staff activities during Rare Disease Week Mackenzie Abramson provides a recap of Rare Disease Day and Rare Disease Week activities in Washington D.C. […] Read more