By James Radke at Rare Disease Report According to the Genetic and Rare Diseases Information Center (GARD) at the National
by Mathew Shanley for Rare Disease Report Earlier today, Takeda and Seattle Genetics announced promising results from its Phase 3 ECHELON-1
Thanks to Rare Disease Report for this piece. University of Southern California (USC) start-up RASRx hopes to develop a drug
Many rare disease parents gain strength and inspiration by watching their ‘disabled’ child adapt because of – and sometimes thrive
By James Radke of Rare Disease Report China is about to publish its first list of national rare diseases.
By Andrew Black at Rare Disease Report She went in to have her tonsil’s removed, she came back with
After 30 years, the Orphan Drug Act is helping small companies innovate in small patient populations. While rare diseases are,
