Catching Up: New Educational Videos, Rare Disease Report Releases Resource Book

November 14, 2014

New videos by Novartis and the GraceWelsey Foundation help to explain complex rare disease. Rare Disease Report releases new resource book for doctors and patients.

Deals

FDA Clears First Trial of Prime Medicine’s Editing Therapy & More — This Week in RARE Daily

This Week in RARE Daily is a feature from Global Genes where you can get a quick […]

Living with a RARE Disease

Shundra Wooten on her short film “Keep It Moving”

Shundra Wooten was diagnosed with Spinocerebellar Ataxia 3, and made a short film “Keep It Moving” to […]

Deals

Profluent Releases AI-Created and Open-Source Gene Editor & More — This Week in RARE Daily

This Week in RARE Daily is a feature from Global Genes where you can get a quick […]

Living with a RARE Disease

Shantel Sonier on “Glitching with Nick”

Shantel Sonier, a rare mom and caregiver to Nick, who was diagnosed with GRIN2A, created the short […]

Living with a RARE Disease

Lesley Holroyd on her short film “Born to be Heard”

Lesley Holroyd, who lives with congenital adrenal hyperplasia, discusses what she learned about filmmaking and telling her […]

Living with a RARE Disease

“Miss Diagnosis” breaking the rules with Tara Rule

Daniel DeFabio, Director of Community Engagement for Global Genes, spoke to Tara Rule about what rules should […]

Genetic

National DNA Day: Cracking the Code on Rare Diseases and Unlocking Hope

by Shruti Mitkus, Ph.D. National DNA Day is celebrated each year on April 25th to commemorate the […]

Deals

Expanding Access to Genome Sequencing in Rural Populations & More — This Week in RARE Daily

This Week in RARE Daily is a feature from Global Genes where you can get a quick […]

Finance

Two Rare Disease Drug Developers Raise Combined $152.5 Million in PIPE Offerings

Rare Daily Staff Two companies developing therapeutics for rare diseases, Zura Bio and Benitec Biopharma, raised $152.5 […]

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Catching Up: New Educational Videos, Rare Disease Report Releases Resource Book

Related

FDA Clears First Trial of Prime Medicine’s Editing Therapy & More — This Week in RARE Daily

Shundra Wooten on her short film “Keep It Moving”

Profluent Releases AI-Created and Open-Source Gene Editor & More — This Week in RARE Daily

Shantel Sonier on “Glitching with Nick”

Lesley Holroyd on her short film “Born to be Heard”

“Miss Diagnosis” breaking the rules with Tara Rule

National DNA Day: Cracking the Code on Rare Diseases and Unlocking Hope

Expanding Access to Genome Sequencing in Rural Populations & More — This Week in RARE Daily

Two Rare Disease Drug Developers Raise Combined $152.5 Million in PIPE Offerings

Stay Connected