Rare Disease Report: Is Eteplirsen Effective in Non-ambulatory Duchenne Patients?

February 1, 2016

Christine McSherry, founder of the Jett Foundation talks about her son’s experience as a non-ambulatory Duchenne muscular dystrophy patient taking Sarepta’s eteplirsen.

SOURCE | RARE DISEASE REPORT

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Rare Disease Report: Is Eteplirsen Effective in Non-ambulatory Duchenne Patients?

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Shundra Wooten on her short film “Keep It Moving”

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