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A total of 11 posts are filed under Science
Learning from Rare Diseases
Daniel S. Levine   Matt Wilsey has liked to make the case that one justification for investing in rare disease research is that through it,… Continue Reading
Gene Editing Technology in Mice Shows Promises as Approach for DMD
Rare Daily Staff Scientists at the University of California, Berkeley have developed a way to deliver gene-editing technology inside cells,… Continue Reading
Study Suggests Existing Drugs Could Treat Rare Bone Cancer
Rare Daily Staff Some patients with chordoma, a rare bone cancer, could benefit from a class of approved drugs known as P13K inhibitors,… Continue Reading
UMass Medical School Gets $10 Million Gift from Li Weibo to Create Rare Diseases Research Institute
Rare Daily Staff The UMass Medical School announced the establishment of the Li Weibo Institute for Rare Diseases Research, an effort to… Continue Reading
FDA Awards Grants for Natural History Studies of Rare Diseases
Rare Daily Staff The U.S. Food and Drug Administration today said it has awarded $6.3 million over the next five years to fund six new… Continue Reading
Grace Science Foundation and Stanford University Create Biobank for Ultra-Rare NGLY1 Deficiency
Rare Daily Staff The Grace Science Foundation and a clinical research team from Stanford University have created an open source biobank of… Continue Reading
Pfizer and African American Newspaper Group Collaborate to Raise Awareness about Sickle Cell Disease
Rare Daily Staff Pfizer and the National Newspaper Publishers Association are collaborating to raise awareness of sickle cell disease, a… Continue Reading