Expert Office Hours

Get one-to-one time with experts on topics such as data collection, research strategy, therapy development, and engaging with the FDA.

Expert Office Hours

Tuesday, April 30, 1pm & 4:30pm
*not all experts are available for all office hours

Get answers to your questions by scheduling a one-to-one session with one of our experts on topics such as data collection, research strategy, therapy development, and engaging with the FDA. Appointments will open in March for registered attendees.

Confirmed attendees may reserve a spot in March.

Lara Bloom
President & CEO
The Ehlers-Danlos Society

Max Bronstein
Executive Director, Government Affairs & Patient Advocacy
Crinetics Pharmaceuticals

Betty Cabrera, MPH
Director of Research Engagement and Operations,
Gene Therapy Center at UCSD

Jennifer Farmer
Friedreich’s Ataxia Research Alliance

Ben Forred, MBA
Director, Translational Research & The CoRDS Registry
Sanford Health

Sharie Haugabook, Ph.D. (with Liz Ottinger, Ph.D.)
Acting Head of Project Management in the Therapeutic Development Branch, Division of Preclinical Innovation

Dave Jacoby, M.D., Ph.D.
Fellow in Clinical Science and Vice President, Head of Discovery Medicine

Dan Lavery

Dan Lavery, Ph.D.
Director of the CDKL5 Program of Excellence
Orphan Disease Center at University of Penn

Juan Carlos Lopez, Ph.D.
Managing Director
RTW Charitable Foundation

Lea Ann Browning McNee
Director of Communication & Engagement
Reagan-Udall Foundation

Casey McPherson
Founder, To Cure A Rose Foundation

Manoj Malhotra, M.D.
Chief Medical Officer
Ovid Therapeutics

Eric Marsh, MD, PhD
Clinical Director, Neurogenetics Program, Associate Professor of Neurology
Children’s Hospital of Pennsylvania

Katherine Maynard
Partner, PWR

Juliane Mills, M.P.H., MS.c.
Strategy Lead
Worldwide Clinical Trials

Liz Ottinger, Ph.D. (with Sharie Haugabook, Ph.D.)
Senior Program Manager Division
Division of Preclinical Innovation, NCATS

Debbie Requesens
Director, JumpStart Program
Orphan Disease Center, University of Pennsylvania

Charlene Son-Rigby, Global Genes CEO

Charlene Son Rigby
CEO, Global Genes

Zohreh Talebizadeh
Senior Director of RARE-X Research Program
Global Genes

Ramona Walls, Ph.D.
Executive Director of Data Science
Critical Path Institute (C-Path)

Cara Weissman

Cara Weismann, Ph.D.
Director for the Program of Excellence
Orphan Disease Center

Ashley Winslow, Ph.D.
Odylia Therapeutics