2022 Rare Disease Drug Development Report: Collaborate to Accelerate

In June 2022, Global Genes partnered with the Orphan Drug Center of the University of Pennsylvania to bring rare disease advocacy leaders, industry representatives, and researchers together at the Rare Drug Development Symposium. The goal of this event was to attendees to openly collaborate, share insights, and learn from each more about the drug development process.

This report summarizes the conversations had during this event. Topics such as:

• Finding a Common Cause.
• Accelerating Rare Disease Research
• The Fastest Way to a New Therapy Can Be an Old One.
• A Framework to Move from Idea to Patient.
• To Innovate Clinical Trials, Focus on Human Behavior.

Download the Report