Tag: Duchenne Muscular Dystrophy

A total of 75 posts are filed under Duchenne Muscular Dystrophy
First Duchenne Muscular Dystrophy Boy in Canada to Begin Drisapersen Redosing
Five years ago, 12-year-old Alex Chiabai was one of the first boy in Canada to begin taking drisapersen, a promising drug that provided a… Continue Reading
RARECast: Summit Pursues A Different Approach to Treating Duchenne
  Duchenne Muscular Dystrophy, a rare genetic disease, causes progressive muscle wasting that slowly robs people of their abilities and… Continue Reading
Rare Disease Report: RASRx is the Latest Duchenne Drug To Get Orphan Status From the FDA
Thanks to Rare Disease Report for this piece. University of Southern California (USC) start-up RASRx hopes to develop a drug to treat… Continue Reading
CD Access to Provide Special Access Program for Duchenne Muscular Dystrophy Patients in Canada
 CD Access is a new nonprofit that provides patients access to drugs and therapies that are currently unavailable through clinical trial… Continue Reading
Michael’s Cause Has Cause for Celebration After Golf Fundraiser
The organization just had their 5th annual UFCW Local 1D/2D Golfing Tournament to raise funds for Duchenne Muscular Dystrophy research.  In… Continue Reading
Leader in Cure, Care and Community for Duchenne Muscular Dystrophy CureDuchenne Launches New Website
CureDuchenne, the leading nonprofit focused on finding a cure for Duchenne muscular dystrophy, launched a new website today… Continue Reading
CureDuchenne Applauds the FDA Approval of Marathon’s EMFLAZA (deflazacort) for the Treatment of Duchenne Muscular Dystrophy
EMFLAZA is the First Drug in the U.S. Approved for Use by Patients Age Five and Older with Duchenne Regardless of Genetic Mutation… Continue Reading