Tag: orphan drugs

A total of 73 posts are filed under orphan drugs
Rare Disease Report: China’s Rare Disease Policy (or Lack Thereof)
By James Radke of Rare Disease Report China is about to publish its first list of national rare diseases.   Given the population of China… Continue Reading
PHRMA.org: More Than 560 Medicines in Development for Rare Diseases
Rare diseases, when taken together, are not that rare at all. In fact, 30 million Americans, or 10 percent of the population, have one of… Continue Reading
RARECast: The Case for Keeping Orphans Where They Can Thrive
  Large pharmaceutical companies have grown increasingly interested in rare diseases, but acquisitions of rare disease companies by large… Continue Reading
Per Patient Costs for Orphan Drugs is 13.8 Times Higher Than Non-Orphan Drugs
With 2020 worldwide sales forecast at $178 billion, the orphan drug market is expected to grow by 11.7 percent per year, (CAGR 2015 to… Continue Reading
Are The Doors of Rare Disease Cures Open Only to the Wealthy–And Can We All Benefit?
This story was originally printed on Genetic Literacy Project. Visit their website here. In Columbia, South Carolina, a couple… Continue Reading
How to Keep the Momentum Going in Orphan Drugs
The passage of the 21st Century Cures Act by the US House of Representatives means that there’s potential for faster drug development in… Continue Reading
RAREcast: How the Orphan Drug Act Reshaped the Rare Disease Landscape
The U.S. Food and Drug Administration approved more than 230 new drugs to treat rare diseases in the past decade and there are currently… Continue Reading