As part of the Becoming a Research Ready Organization track from the 2023 RARE Advocacy Summit, this session will ensure you have essential elements in place to allow experimental therapies to advance to clinical trials. Topics include conducting natural history studies, identifying and validating biomarkers, determining appropriate endpoints, disease concept models and regulatory strategies.
Becoming Clinical Trial Ready
Moderator:
Christina Saninocencio, PhD, CPH, CNP
Founder, LGS Foundation; Lecturer, Fairfield University
Panelists:
* Kendall Davis, MPH
Director of Advocacy and Engagement, ICON, plc
* Brian Pfister
VP, Global Medical Affairs Lead, Praxis Precision Medicines
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