Tag: Duchenne

A total of 14 posts are filed under Duchenne
RARECast: Marathon Preps DMD Drug for FDA
While much of the attention of the Duchenne Muscular Dystrophy community has been focused on the recent FDA advisory committee review of… Continue Reading
PTC Announces Results from Phase 3 ACT DMD Clinical Trial of TranslarnaTM (ataluren) in Patients with Duchenne Muscular Dystrophy
PTC Therapeutics, Inc. recently announced results from the Phase 3, double-blind, placebo-controlled, 48-week ACT DMD trial of TranslarnaTM… Continue Reading
Biomarin Launches kNOWyourDuchenne Program Offering Genetic Testing
BioMarin has officially launched kNOWyourDuchenne, a program dedicated to assisting families and clinicians gain access to genetic testing… Continue Reading
Struggling to Run Around on the Playground, 9-Year-Old Recieves Startling Diagnosis
Michael Capolongo at the age of 4 was complaining of leg pain when running around the playground with his pre K classmates. His pediatrician… Continue Reading
Duchenne Community Finds Hope in Anaheim Ducks Captain Ryan Getzlaf and Hawken Miller
As Ryan Getzlaf loads a baby seat into the trunk of his white Mercedes S63, a pack of young fans swarms him in hopes of an autograph, a… Continue Reading
Pfizer Initiates Phase 2 Study of PF-06252616 in Duchenne Muscular Dystrophy
Pfizer Inc. (NYSE:PFE) announced today enrollment of the first patient in a multicenter Phase II clinical trial of the investigational… Continue Reading
Parent Project Muscular Dystrophy Names Baltimore’s Kennedy Krieger Institute a Certified Duchenne Care Center
 Kennedy Krieger Institute in Baltimore, Maryland was named a Certified Duchenne Care Center by Parent Project Muscular Dystrophy… Continue Reading
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