Sessions from Track 4: RARE Disease Masterclass: Science & Tech Innovation will be live streamed here September 19 and 20, and may be watched on demand in October.

Sessions from other tracks will be available to view by clicking the links below:

Help rare disease patients more effectively navigate the world of healthcare and legislative action

Help rare disease organizations expand their reach and improve their effectiveness

Help patient advocacy groups develop and execute a research agenda to accelerate the development of therapies

Hear from drug development experts guiding rare disease advocates through the different therapeutic modalities

* Please note that some sessions listed on the agenda are networking or one-on-one opportunities, and are not available to live stream.

Thinking Like a Researcher: Disease Biology 101
Tuesday, September 19, 2:15-3:00pm PT / 5:15-6:00pm ET

Small Molecules, Drug Repurposing and Biologics
Tuesday, September 19, 3:15-4:00pm PT / 6:15-7:00pm ET

RNA Therapies: ASOs, mRNAs, siRNAs
Tuesday, September 19, 4:15-5:00pm PT / 7:15-8:00pm ET

Gene Replacement and Gene Editing Therapies
Wednesday, September 20, 10:00-10:45am PT / 1:00-1:45pm ET

Spinal Muscular Atrophy Case Study
Wednesday, September 20, 11:00-11:45am PT / 2:00-2:45pm ET

How Companies Decide Which Therapies to Pursue
Wednesday, September 20, 2:00-2:45pm PT / 5:00-5:45pm ET

7 Ways to Engage the FDA
Wednesday, September 20, 3:00-3:45pm PT / 6:00-6:45pm ET