Dive into a community of rare disease patients, caregivers, advocates, and partners from around the world, connected by one passion – improving the lives of people with rare disease.

Community Highlights

January 25, 2022
Finding Answers Through Genetic Testing – A Personal Journey
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January 25, 2022
Metagenomi Raises $175 Million to Advance Therapeutic Pipeline and Expand Gene Editing Platform
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January 25, 2022
FDA Grants Evrysdi Priority Review Based on Results from Treating Pre-Symptomatic Infants with SMA
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