Dive into a community of rare disease patients, caregivers, advocates, and partners from around the world, connected by one passion – improving the lives of people with rare disease.

Community Highlights

December 2, 2021
Rare Leader: Megan Golden, CEO and Co-Founder, Mission: Cure
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December 2, 2021
AviadoBio Raises $80 million to Advance Neurodegenerative Gene Therapy Platform
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December 2, 2021
Krystal Biotech Raises $200 Million in Public Offering to Advance Redosable Gene Therapies
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