Dive into a community of rare disease patients, caregivers, advocates, and partners from around the world, connected by one passion – improving the lives of people with rare disease.

Community Highlights

December 7, 2022
Enzyvant Merges with Altavant to Advance Therapies for Rare Diseases in Immunology and Cardiopulmonology
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December 7, 2022
PacBio and Boston Children’s Collaborate to Investigate Novel Variants Inaccessible by Short-Read Sequencing
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December 7, 2022
Neurocrine’s Experimental Therapy for EE Fails to Meet Endpoint in Phase 2 Study
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